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Peroxisomal Disorders

Showing 1 - 25 of >10,000

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Patients With Peroxisome Biogenesis Disorders (PBD)

Recruiting
  • Peroxisome Biogenesis Disorder
  • +10 more
    • Montreal, Quebec, Canada
      Research Institute of the McGill University Health Center
    Jul 4, 2022

    Protein Translocation in Patients With Beta-Oxidation Disorders

    Completed
    • Beta-Oxidation Disorder
    • Peroxisomal Disorders
      • (no location specified)
      Sep 21, 2021

      Mucopolysaccharidosis Disorders, Hurler Syndrome, Hunter Syndrome Trial in Minneapolis (Stem Cell Transplantation, IMD

      Recruiting
      • Mucopolysaccharidosis Disorders
      • +28 more
      • Stem Cell Transplantation
      • +7 more
      • Minneapolis, Minnesota
        Masonic Cancer Center, University of Minnesota
      Nov 1, 2022

      Mitochondrial and Peroxisomal Metabolism to Differentiate

      Recruiting
      • Idiopathic Parkinson Disease
      • Parkinsonian Syndrome
      • blood collection
      • Dijon, France
        Chu Dijon Bourgogne
      Oct 26, 2021

      Leukodystrophy, White Matter Disease, Leukoencephalopathies Trial in United States

      Recruiting
      • Leukodystrophy
      • +21 more
        • Palo Alto, California
        • +8 more
        Dec 21, 2021

        New Strategy for the Diagnosis of Peroxisomal Diseases

        Recruiting
        • Peroxisomal Disorders
        • Diagnoses Disease
          • Amiens, France
          • +3 more
          Aug 24, 2020

          Infantile Refsum's Disease, Zellweger Syndrome, Adrenoleukodystrophy Trial in Cincinnati (Cholic Acids)

          Completed
          • Infantile Refsum's Disease
          • +4 more
          • Cholic Acids
          • Cincinnati, Ohio
            Cincinnati Children's Hospital Medical Center
          Sep 28, 2020

          Incidence of Metabolic Disorders in Neonatal Convulsions

          Not yet recruiting
          • Neonatal Convulsions
          • MRI
          • (no location specified)
          Nov 6, 2023

          X-linked Adrenoleukodystrophy Trial in Leipzig (SMART-ALD, Waiting list)

          Recruiting
          • X-linked Adrenoleukodystrophy
          • SMART-ALD
          • Waiting list
          • Leipzig, Saxony, Germany
          • +1 more
          Aug 16, 2022

          Quality of Life in Women With X-linked Adrenoleukodystrophy

          Recruiting
          • X-linked Adrenoleukodystrophy
            • Leipzig, Saxony, Germany
              Leipzig University Medical Center, Leukodystrophy Outpatient Cli
            Apr 4, 2022

            AMN, AMN Gene Mutation, X-ALD Trial in Worcester (SBT101, Imitation Procedure)

            Recruiting
            • AMN
            • +2 more
            • SBT101
            • Imitation Procedure
            • Worcester, Massachusetts
              University of Massachusetts Chan Medical School
            Jun 1, 2022

            Adrenoleukodystrophy, Metachromatic Leukodystrophy, Globoid Cell Leukodystrophy Trial in Minneapolis (drug, procedure,

            Completed
            • Adrenoleukodystrophy
            • +8 more
            • Minneapolis, Minnesota
              Masonic Cancer Center, University of Minnesota
            Jul 10, 2019

            Zellweger Syndrome, Peroxisome Biogenesis Disorders Trial in Toronto (Hydroxychloroquine, Placebo)

            Completed
            • Zellweger Syndrome
            • Peroxisome Biogenesis Disorders
            • Toronto, Ontario, Canada
              The Hospital for Sick Children
            Dec 15, 2020

            Metabolic Diseases Trial in Pittsburgh (human hepatocyte transplantation, Preparative Radiation Therapy)

            Suspended
            • Metabolic Diseases
            • human hepatocyte transplantation
            • Preparative Radiation Therapy
            • Pittsburgh, Pennsylvania
              Children's Hospital of Pittsburgh of UPMC
            Jan 6, 2022

            Biomarkers for Inborn Errors of Metabolism

            Completed
            • Inborn Errors of Metabolism
            • Biomarker
              • Tirana, Albania
              • +12 more
              Mar 23, 2022

              Leukodystrophy: An Observational Study at Sohag University

              Not yet recruiting
              • Children With Leukodystrophy
              • MRI
              • (no location specified)
              Mar 2, 2021

              Rhizomelic Chondrodysplasia Punctata Trial in Toronto (PPI-1011, Placebo)

              Recruiting
              • Rhizomelic Chondrodysplasia Punctata
              • Toronto, Ontario, Canada
                Biopharma Services Inc.
              Jul 23, 2023

              Mental Disorders: Application of a Multi-modal & Domains System

              Not yet recruiting
              • Mental Disorder
                • Shanghai, Shanghai, China
                  Shanghai Mental Health Center
                Jul 2, 2023

                "Functional Overlay" in Patients With Movement Disorders

                Recruiting
                • Conversion Disorder
                • +3 more
                • Neurological examination
                • +4 more
                • Graz, Styria, Austria
                  Medical University of graz
                Jul 5, 2023

                Anxiety Disorder, Depressive Disorder Trial (Dialectical behavior therapy (DBT))

                Not yet recruiting
                • Anxiety Disorder
                • Depressive Disorder
                • Dialectical behavior therapy (DBT)
                • (no location specified)
                Aug 13, 2023

                Oral Disorder Trial in Paris (Psychological care)

                Not yet recruiting
                • Oral Disorder
                • Psychological care
                • Paris, France
                  Robert Debre Hospital
                Sep 19, 2023

                Depression ,Anxiety and Stress Disorders Among Diabetic Assuit

                Not yet recruiting
                • Diabetes Mellitus
                  • (no location specified)
                  Sep 30, 2023

                  Depressive Disorder, AD, ASD Trial in Chongqing (functional training, Observation)

                  Recruiting
                  • Depressive Disorder
                  • +3 more
                  • functional training
                  • Observation
                  • Chongqing, Chongqing, China
                    Growth,Development and Mental Health of Children and Adolescents
                  Nov 23, 2023

                  Hematological Disorder in Patients With Angiodysplasia

                  Not yet recruiting
                  • Angiodysplasia
                  • Hematological Disease
                  • Von willebrand antigen
                  • (no location specified)
                  Sep 26, 2023

                  Lysosomal Storage Disease, Peroxisomal Disorder Trial in Minneapolis (drug, radiation, biological)

                  Completed
                  • Lysosomal Storage Disease
                  • Peroxisomal Disorder
                  • Minneapolis, Minnesota
                    Masonic Cancer Center, University of Minnesota
                  Dec 3, 2017